Gene therapy treatments for rare diseases are being developed, but getting them out of the lab has proved challenging.

Like other developing countries, Indonesia is facing a familiar dilemma: how to feed a growing population while protecting ...

Researchers have developed a gene editing strategy that could repair the genetic problems that lead to Huntington's disease and Friedreich's ataxia. These disorders arise because of abnormal repeats ...

The need to change regulations around gene-editing treatments was endorsed in November by the head of the US Food and Drug ...

Scientists discovered that aging DNA repeats expand at wildly different speeds—and in some people, the consequences can be devastating. A sweeping genetic study drawing on data from more than 900,000 ...

Metabolic dysfunction-associated steatotic liver disease (MASLD) affects nearly one in three adults around the globe. It starts when fat builds up inside the liver’s cells. Over time, this buildup can ...

TUCSON, Ariz. (KGUN) — Hudson Sanford is a seven-year-old boy that was diagnosed with Duchenne muscular dystrophy (DMD) when he was four years old. World Duchenne Awareness Day is celebrated on ...

Researchers at UCLA Health have found that a person's risk of developing psychotic-like experiences may be influenced by both childhood attention problems and their genetic makeup. The findings, ...

Genetics play a role in low testosterone for some men, but underlying causes vary widely. Many genes influence testosterone ...

Some gene therapies are very expensive to manufacture. Those difficulties caused one developer to exit the E.U. market. Several leading companies will need to wrangle with the issue to succeed. Most ...